本レポートは、ホモ接合性家族性高コレステロール血症(HoFH)の臨床試験シナリオの概要を説明し、ホモ接合性家族性高コレステロール血症(HoFH)に関する臨床試験に関連するトップラインデータを提供します。本レポートは、世界の首位諸国における臨床試験件数および平均被験者数などに注目し、ホモ接合性家族性高コレステロール血症(HoFH)の臨床試験の概要を提供します。また、地域別、国別(G7 & E7)、段階別、進捗状況別、臨床試験の目標の達成状況別、スポンサーの種類別に、ホモ接合性家族性高コレステロール血症(HoFH)の臨床試験を分析します。さらに、臨床試験が進行中の主要薬剤の情報(進行中の臨床試験数に基づく)を提供します。
本レポートは、GlobalData社の社内データベース(Pharma - 臨床試験データベース)から入手したデータを用いて作成されています。臨床試験は、世界の80を超えるさまざまな臨床試験レジストリ、会議、ジャーナル、ニュースなどから照合されています。臨床試験データベースは、ダイナミックなプロセスによって周期的に更新されます。
目次
Table of Contents
Table of Contents
List of Tables
List of Figures
Introduction
Global Markets Direct Report Coverage
Homozygous Familial Hypercholesterolemia (HoFH) - Overview
Homozygous Familial Hypercholesterolemia (HoFH) - Therapeutics Development
Pipeline Overview
Pipeline by Companies
Products under Development by Companies
Homozygous Familial Hypercholesterolemia (HoFH) - Therapeutics Assessment
Assessment by Target
Assessment by Mechanism of Action
Assessment by Route of Administration
Assessment by Molecule Type
Homozygous Familial Hypercholesterolemia (HoFH) - Companies Involved in Therapeutics Development
AD Pharmaceuticals Co Ltd
Amryt Pharma Plc
Beijing Mabworks Biotech Co Ltd
Daewoong Co Ltd
Gemphire Therapeutics Inc
Innovent Biologics Inc
LIB Therapeutics LLC
Lipigon Pharmaceuticals AB
LipimetiX Development Inc
Madrigal Pharmaceuticals Inc
Pfizer Inc
Regeneron Pharmaceuticals Inc
RegenxBio Inc
The Medicines Company
Homozygous Familial Hypercholesterolemia (HoFH) - Drug Profiles
Homozygous Familial Hypercholesterolemia (HoFH) - Dormant Projects
Homozygous Familial Hypercholesterolemia (HoFH) - Discontinued Products
Homozygous Familial Hypercholesterolemia (HoFH) - Product Development Milestones
Appendix
List of Tables
Number of Products under Development for Homozygous Familial Hypercholesterolemia (HoFH), H2 2019
Number of Products under Development by Companies, H2 2019
Products under Development by Companies, H2 2019
Products under Development by Companies, H2 2019 (Contd..1), H2 2019
Number of Products by Stage and Target, H2 2019
Number of Products by Stage and Mechanism of Action, H2 2019
Number of Products by Stage and Route of Administration, H2 2019
Number of Products by Stage and Molecule Type, H2 2019
Homozygous Familial Hypercholesterolemia (HoFH) - Pipeline by AD Pharmaceuticals Co Ltd, H2 2019
Homozygous Familial Hypercholesterolemia (HoFH) - Pipeline by Amryt Pharma Plc, H2 2019
Homozygous Familial Hypercholesterolemia (HoFH) - Dormant Projects, H2 2019
Homozygous Familial Hypercholesterolemia (HoFH) - Discontinued Products, H2 2019
List of Figures
Number of Products under Development for Homozygous Familial Hypercholesterolemia (HoFH), H2 2019
Number of Products under Development by Companies, H2 2019
Number of Products by Targets, H2 2019
Number of Products by Stage and Top 10 Targets, H2 2019
Number of Products by Mechanism of Actions, H2 2019
Number of Products by Stage and Mechanism of Actions, H2 2019
Number of Products by Routes of Administration, H2 2019
Number of Products by Stage and Routes of Administration, H2 2019
Number of Products by Molecule Types, H2 2019
Number of Products by Stage and Molecule Types, H2 2019